Clinical Trial ID NCT01826487, A Phase 3 Efficacy and Safety Study of Ataluren (PTC124(R)) in Patients With Nonsense Mutation Dystrophinopathy, Principal Investigator
Clinical Trial ID NCT01540409, Open Label, Multiple-Dose Efficacy, Safety, and Tolerability Study of Eteplirsen in Patients with Duchenne Muscular Dystrophy who participated in Study 4658-US-201, Principal Investigator
A Phase 3 Extension Study of Ataluren (PTC124) in Patients with Nonsense Mutation Dystrophinopathy, Principal Investigator